Videos & Voices

Joyce, an actual Galafold patient.

Real Patients, Real Stories

Hear from members of the Galafold® (migalastat) community about their journeys to diagnosis and to getting on Galafold. You'll also learn how each one of them finds different ways to fit Galafold into their individual lifestyles.

Meet Rebecca

For years, Rebecca thought her stomach issues and vertigo were caused by stress. But when her son started to experience similar symptoms, she sought out a genetic counselor, who confirmed that they had Fabry disease. From there, Rebecca went on to participate in the Galafold clinical trial and has been on Galafold ever since.

Meet Anthony

When Anthony first started having health issues as a kid—feet and hands burning during soccer—he assumed they were normal and would come and go. But throughout his teenage years, his symptoms worsened. Anthony and his mom were outspoken in their quest for answers. It was Fabry. After hearing about Galafold as an adult, his original childhood diagnosis was re-reviewed. It was determined that he was amenable for Galafold.

Meet Joyce

Growing up, Joyce and her siblings experienced the same unexplained symptoms. But after 2 of her brothers were diagnosed with Fabry disease, Joyce knew it was time to see a genetic counselor. From there, she was enrolled in the Galafold trial and continues to take Galafold to treat her Fabry to this day.

Meet Alex

On his journey towards a Fabry diagnosis, Alex was misdiagnosed many times along the way. But as his symptoms continued to worsen, Alex and his wife were persistent in getting to the bottom of it. Eventually, Alex was diagnosed with Fabry disease and was the first person to take Galafold as a part of the clinical trials. In his words, Alex "learned how to take Galafold so that it worked for me."

A Journey Through Fabry and Galafold

How Galafold Works

Watch how Galafold acts as a pharmacological chaperone if you have an amenable GLA gene variant.

INDICATION AND IMPORTANT SAFETY INFORMATION

Before taking Galafold® (migalastat), tell your healthcare provider about all of your medical conditions, including if you:

  • have kidney problems.
  • are pregnant or plan to become pregnant. It is not known if Galafold will harm your unborn baby.
  • have kidney problems.
  • are pregnant or plan to become pregnant. It is not known if Galafold will harm your unborn baby.
  • are breastfeeding or plan to breastfeed. Galafold may pass into breast milk. Talk to your healthcare provider
    about the best way to feed your baby if you take Galafold.

Tell your healthcare provider about all the medicines you take, including prescription and over-the-counter medicines, vitamins, and herbal supplements.

What are the possible side effects of Galafold?

The most common side effects of Galafold include headache, stuffy or runny nose and sore throat, urinary tract infection, nausea, and fever.

These are not all the possible side effects of Galafold. Call your healthcare provider for medical advice about side effects.

What is Galafold?

Galafold is a prescription medicine used to treat adults with Fabry disease who have a certain genetic change (variant) in the galactosidase alpha gene (GLA) that is responsive (amenable) to Galafold.

It is not known if Galafold is safe and effective in children.

You may report side effects to FDA at 1-800-FDA-1088. You may also report side effects to Amicus Therapeutics at 1-877-4AMICUS.

Please click here for Full Prescribing Information, including Patient Information and Instructions for Use.